Calendario›SNY›A Prospective, Observational Study in Patients With Late-Onset Pompe Disease
A Prospective, Observational Study in Patients With Late-Onset Pompe Disease
Ensayo de Sanofi en Glycogen Storage Disease Type II (del registro, en inglés).
- Fase
- no aplica
- Estado
- Completado
- Participantes
- 61
- Centros
- 5
- Fin del objetivo primario
- may 2005
previstos
fecha real
Qué significa cada fase y cada estado.
Estudio observacional. Comenzó en mar 2004.
Cómo lo describe el promotor
En el documentoEn inglés, del registroPompe disease (also known as glycogen storage disease type II, "GSD-II") is caused by a deficiency of a critical enzyme in the body called acid alpha-glucosidase (GAA). Normally, GAA is used by the body's cells to break down glycogen (a stored form of sugar) within specialized structures called lysosomes. In patients with Pompe disease, an excessive amount of glycogen accumulates and is stored in various tissues, especially heart and skeletal muscle, which prevents their normal function. This study is being conducted to collect prospective, observational data on patients with late-onset Pompe disease. Approximately 60 subjects with late-onset Pompe disease will be enrolled.
Más ensayos de SNY
| Ensayo | Fase | Estado | Lectura de resultados |
|---|---|---|---|
| Avalglucosidase alfa · Mini-COMET | Fase 2 | En marcha, sin reclutar | sep 2019 (real) |
| Yellow fever vaccine | Fase 2 | En marcha, sin reclutar | may 2022 (real) |
| Yellow fever vaccine · VYF02 | Fase 2 | En marcha, sin reclutar | jun 2022 (real) |
| SAR441344 IV | Fase 2 | En marcha, sin reclutar | sep 2022 (real) |
| Meningococcal Polysaccharide | Fase 3 | En marcha, sin reclutar | mar 2023 (real) |
| Isatuximab IV · IRAKLIA | Fase 3 | En marcha, sin reclutar | nov 2024 (real) |
Todos los de SNY, en su ficha.
Ficha completa en ClinicalTrials.gov (NCT00077662), actualizada en may 2015.